BioSpace

FDA nod for Mirum’s Atebrioz makes 3 options for ultra-rare bone disease

The approval of Mirum Pharmaceuticals’ ALK2 inhibitor for fibrodysplasia ossificans progressiva on Friday adds a third option for patients who had long been without any treatments, joining Regeneron’s recently approved Pasatru and Ipsen’s Sohonos.

作者 BioSpace

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FDA nod for Mirum’s Atebrioz makes 3 options for ultra-rare bone disease
FDA nod for Mirum’s Atebrioz makes 3 options for ultra-rare bone disease

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